Global Hemophilia Gene Therapy Market Growth (Status and Outlook) 2019-2024
Report ID: 92080 | Feb 2019 | No. of Pages: 119
Hemophilia is a rare bleeding disorder in which the blood does not clot normally. Hemophilia is a monogenic disease (a disease that is caused by a genetic defect in a single gene). There are two types of hemophilia caused by mutations in genes that encode protein factors which help the blood clot and stop bleeding when blood vessels are injured. Individuals with hemophilia experience bleeding episodes after injuries and spontaneous bleeding episodes that often lead to joint disease such as arthritis. The most frequent forms of hemophilia affect males.
About 80% of them have hemophilia A, which affects the clotting factor VIII. The second most common form, hemophilia B, is due to a deficiency of the clotting factor IX. Several biotechs are racing to launch the first gene therapy for hemophilia. Currently, uniQure in the Netherlands and Spark Therapeutics in the US have the most advanced programs. Spark scored a victory in December when it presented Phase I/II for its candidate SPK-9001. The gene therapy was able to reduce annual bleeding episodes by 97%, as compared to its competitor uniQure's candidate, AMT-060. However, uniQure has fought back. The company added a modification in its gene therapy that is known to increase clotting activity by 8- to 9- fold. This improved version has already been cleared to start a Phase III clinical trial in both Europe and the US.
Hemophilia B has traditionally been the main focus of biotechs, since most big pharma efforts were focused on the bigger hemophilia A market. In addition, applying gene therapy to hemophilia A is more challenging; The gene coding for the factor IX protein missing in hemophilia B is simply smaller than that for factor VIII missing in hemophilia A, and therefore easier to fit in the viral vectors used for gene delivery. US-based BioMarin is leading the development of a gene therapy. To overcome the size limit, the company has deleted a region from the factor VIII protein that is not necessary for clotting.
Hemophilia treatment is currently in the pre-clinical stage. And the multiple treatments that are underway might significantly improve the quality of life of patients with hemophilia, by getting rid of frequent infusions and hospital visits, and transitioning patients from severe to mild hemophilia.

According to this study, over the next five years the Hemophilia Gene Therapy market will register a xx% CAGR in terms of revenue, the global market size will reach US$ xx million by 2024, from US$ xx million in 2019. In particular, this report presents the global revenue market share of key companies in Hemophilia Gene Therapy business, shared in Chapter 3.

This report presents a comprehensive overview, market shares and growth opportunities of Hemophilia Gene Therapy market by product type, application, key companies and key regions.

This study considers the Hemophilia Gene Therapy value generated from the sales of the following segments:

Segmentation by product type: breakdown data from 2014 to 2019 in Section 2.3; and forecast to 2024 in section 10.7.
Hemophilia A
Hemophilia B
Segmentation by application: breakdown data from 2014 to 2019, in Section 2.4; and forecast to 2024 in section 10.8.
Hemophilia A Gene Therapy
Hemophilia B Gene Therapy

This report also splits the market by region: Breakdown data in Chapter 4, 5, 6, 7 and 8.
Americas
United States
Canada
Mexico
Brazil
APAC
China
Japan
Korea
Southeast Asia
India
Australia
Europe
Germany
France
UK
Italy
Russia
Spain
Middle East & Africa
Egypt
South Africa
Israel
Turkey
GCC Countries

The report also presents the market competition landscape and a corresponding detailed analysis of the major vendor/manufacturers in the market. The key manufacturers covered in this report: Breakdown data in in Chapter 3.
Spark Therapeutics
Ultragenyx
Shire PLC
Sangamo Therapeutics
Bioverativ
BioMarin
uniQure
Freeline Therapeutics

In addition, this report discusses the key drivers influencing market growth, opportunities, the challenges and the risks faced by key players and the market as a whole. It also analyzes key emerging trends and their impact on present and future development.

Research objectives
To study and analyze the global Hemophilia Gene Therapy market size by key regions/countries, product type and application, history data from 2014 to 2018, and forecast to 2024.
To understand the structure of Hemophilia Gene Therapy market by identifying its various subsegments.
Focuses on the key global Hemophilia Gene Therapy players, to define, describe and analyze the value, market share, market competition landscape, SWOT analysis and development plans in next few years.
To analyze the Hemophilia Gene Therapy with respect to individual growth trends, future prospects, and their contribution to the total market.
To share detailed information about the key factors influencing the growth of the market (growth potential, opportunities, drivers, industry-specific challenges and risks).
To project the size of Hemophilia Gene Therapy submarkets, with respect to key regions (along with their respective key countries).
To analyze competitive developments such as expansions, agreements, new product launches and acquisitions in the market.
To strategically profile the key players and comprehensively analyze their growth strategies.
Table of Contents

2019-2024 Global Hemophilia Gene Therapy Market Report (Status and Outlook)

1 Scope of the Report
1.1 Market Introduction
1.2 Research Objectives
1.3 Years Considered
1.4 Market Research Methodology
1.5 Economic Indicators
1.6 Currency Considered

2 Executive Summary
2.1 World Market Overview
2.1.1 Global Hemophilia Gene Therapy Market Size 2014-2024
2.1.2 Hemophilia Gene Therapy Market Size CAGR by Region
2.2 Hemophilia Gene Therapy Segment by Type
2.2.1 Hemophilia A
2.2.2 Hemophilia B
2.3 Hemophilia Gene Therapy Market Size by Type
2.3.1 Global Hemophilia Gene Therapy Market Size Market Share by Type (2014-2019)
2.3.2 Global Hemophilia Gene Therapy Market Size Growth Rate by Type (2014-2019)
2.4 Hemophilia Gene Therapy Segment by Application
2.4.1 Hemophilia A Gene Therapy
2.4.2 Hemophilia B Gene Therapy
2.5 Hemophilia Gene Therapy Market Size by Application
2.5.1 Global Hemophilia Gene Therapy Market Size Market Share by Application (2014-2019)
2.5.2 Global Hemophilia Gene Therapy Market Size Growth Rate by Application (2014-2019)

3 Global Hemophilia Gene Therapy by Players
3.1 Global Hemophilia Gene Therapy Market Size Market Share by Players
3.1.1 Global Hemophilia Gene Therapy Market Size by Players (2017-2019)
3.1.2 Global Hemophilia Gene Therapy Market Size Market Share by Players (2017-2019)
3.2 Global Hemophilia Gene Therapy Key Players Head office and Products Offered
3.3 Market Concentration Rate Analysis
3.3.1 Competition Landscape Analysis
3.3.2 Concentration Ratio (CR3, CR5 and CR10) (2017-2019)
3.4 New Products and Potential Entrants
3.5 Mergers & Acquisitions, Expansion

4 Hemophilia Gene Therapy by Regions
4.1 Hemophilia Gene Therapy Market Size by Regions
4.2 Americas Hemophilia Gene Therapy Market Size Growth
4.3 APAC Hemophilia Gene Therapy Market Size Growth
4.4 Europe Hemophilia Gene Therapy Market Size Growth
4.5 Middle East & Africa Hemophilia Gene Therapy Market Size Growth

5 Americas
5.1 Americas Hemophilia Gene Therapy Market Size by Countries
5.2 Americas Hemophilia Gene Therapy Market Size by Type
5.3 Americas Hemophilia Gene Therapy Market Size by Application
5.4 United States
5.5 Canada
5.6 Mexico
5.7 Key Economic Indicators of Few Americas Countries

6 APAC
6.1 APAC Hemophilia Gene Therapy Market Size by Countries
6.2 APAC Hemophilia Gene Therapy Market Size by Type
6.3 APAC Hemophilia Gene Therapy Market Size by Application
6.4 China
6.5 Japan
6.6 Korea
6.7 Southeast Asia
6.8 India
6.9 Australia
6.10 Key Economic Indicators of Few APAC Countries

7 Europe
7.1 Europe Hemophilia Gene Therapy by Countries
7.2 Europe Hemophilia Gene Therapy Market Size by Type
7.3 Europe Hemophilia Gene Therapy Market Size by Application
7.4 Germany
7.5 France
7.6 UK
7.7 Italy
7.8 Russia
7.9 Spain
7.10 Key Economic Indicators of Few Europe Countries

8 Middle East & Africa
8.1 Middle East & Africa Hemophilia Gene Therapy by Countries
8.2 Middle East & Africa Hemophilia Gene Therapy Market Size by Type
8.3 Middle East & Africa Hemophilia Gene Therapy Market Size by Application
8.4 Egypt
8.5 South Africa
8.6 Israel
8.7 Turkey
8.8 GCC Countries

9 Market Drivers, Challenges and Trends
9.1 Market Drivers and Impact
9.1.1 Growing Demand from Key Regions
9.1.2 Growing Demand from Key Applications and Potential Industries
9.2 Market Challenges and Impact
9.3 Market Trends

10 Global Hemophilia Gene Therapy Market Forecast
10.1 Global Hemophilia Gene Therapy Market Size Forecast (2019-2024)
10.2 Global Hemophilia Gene Therapy Forecast by Regions
10.2.1 Global Hemophilia Gene Therapy Forecast by Regions (2019-2024)
10.2.2 Americas Market Forecast
10.2.3 APAC Market Forecast
10.2.4 Europe Market Forecast
10.2.5 Middle East & Africa Market Forecast
10.3 Americas Forecast by Countries
10.3.1 United States Market Forecast
10.3.2 Canada Market Forecast
10.3.3 Mexico Market Forecast
10.3.4 Brazil Market Forecast
10.4 APAC Forecast by Countries
10.4.1 China Market Forecast
10.4.2 Japan Market Forecast
10.4.3 Korea Market Forecast
10.4.4 Southeast Asia Market Forecast
10.4.5 India Market Forecast
10.4.6 Australia Market Forecast
10.5 Europe Forecast by Countries
10.5.1 Germany Market Forecast
10.5.2 France Market Forecast
10.5.3 UK Market Forecast
10.5.4 Italy Market Forecast
10.5.5 Russia Market Forecast
10.5.6 Spain Market Forecast
10.6 Middle East & Africa Forecast by Countries
10.6.1 Egypt Market Forecast
10.6.2 South Africa Market Forecast
10.6.3 Israel Market Forecast
10.6.4 Turkey Market Forecast
10.6.5 GCC Countries Market Forecast
10.7 Global Hemophilia Gene Therapy Forecast by Type
10.8 Global Hemophilia Gene Therapy Forecast by Application

11 Key Players Analysis
11.1 Spark Therapeutics
11.1.1 Company Details
11.1.2 Hemophilia Gene Therapy Product Offered
11.1.3 Spark Therapeutics Hemophilia Gene Therapy Revenue, Gross Margin and Market Share (2017-2019)
11.1.4 Main Business Overview
11.1.5 Spark Therapeutics News
11.2 Ultragenyx
11.2.1 Company Details
11.2.2 Hemophilia Gene Therapy Product Offered
11.2.3 Ultragenyx Hemophilia Gene Therapy Revenue, Gross Margin and Market Share (2017-2019)
11.2.4 Main Business Overview
11.2.5 Ultragenyx News
11.3 Shire PLC
11.3.1 Company Details
11.3.2 Hemophilia Gene Therapy Product Offered
11.3.3 Shire PLC Hemophilia Gene Therapy Revenue, Gross Margin and Market Share (2017-2019)
11.3.4 Main Business Overview
11.3.5 Shire PLC News
11.4 Sangamo Therapeutics
11.4.1 Company Details
11.4.2 Hemophilia Gene Therapy Product Offered
11.4.3 Sangamo Therapeutics Hemophilia Gene Therapy Revenue, Gross Margin and Market Share (2017-2019)
11.4.4 Main Business Overview
11.4.5 Sangamo Therapeutics News
11.5 Bioverativ
11.5.1 Company Details
11.5.2 Hemophilia Gene Therapy Product Offered
11.5.3 Bioverativ Hemophilia Gene Therapy Revenue, Gross Margin and Market Share (2017-2019)
11.5.4 Main Business Overview
11.5.5 Bioverativ News
11.6 BioMarin
11.6.1 Company Details
11.6.2 Hemophilia Gene Therapy Product Offered
11.6.3 BioMarin Hemophilia Gene Therapy Revenue, Gross Margin and Market Share (2017-2019)
11.6.4 Main Business Overview
11.6.5 BioMarin News
11.7 uniQure
11.7.1 Company Details
11.7.2 Hemophilia Gene Therapy Product Offered
11.7.3 uniQure Hemophilia Gene Therapy Revenue, Gross Margin and Market Share (2017-2019)
11.7.4 Main Business Overview
11.7.5 uniQure News
11.8 Freeline Therapeutics
11.8.1 Company Details
11.8.2 Hemophilia Gene Therapy Product Offered
11.8.3 Freeline Therapeutics Hemophilia Gene Therapy Revenue, Gross Margin and Market Share (2017-2019)
11.8.4 Main Business Overview
11.8.5 Freeline Therapeutics News

12 Research Findings and Conclusion


List of Tables and Figures

Table Product Specifications of Hemophilia Gene Therapy
Figure Hemophilia Gene Therapy Report Years Considered
Figure Market Research Methodology
Figure Global Hemophilia Gene Therapy Market Size Growth Rate 2014-2024 ($ Millions)
Table Hemophilia Gene Therapy Market Size CAGR by Region 2014-2024 ($ Millions)
Table Major Players of Hemophilia A
Table Major Players of Hemophilia B
Table Market Size by Type (2014-2019) ($ Millions)
Table Global Hemophilia Gene Therapy Market Size Market Share by Type (2014-2019)
Figure Global Hemophilia Gene Therapy Market Size Market Share by Type (2014-2019)
Figure Global Hemophilia A Market Size Growth Rate
Figure Global Hemophilia B Market Size Growth Rate
Figure Hemophilia Gene Therapy Consumed in Hemophilia A Gene Therapy
Figure Global Hemophilia Gene Therapy Market: Hemophilia A Gene Therapy (2014-2019) ($ Millions)
Figure Global Hemophilia A Gene Therapy YoY Growth ($ Millions)
Figure Hemophilia Gene Therapy Consumed in Hemophilia B Gene Therapy
Figure Global Hemophilia Gene Therapy Market: Hemophilia B Gene Therapy (2014-2019) ($ Millions)
Figure Global Hemophilia B Gene Therapy YoY Growth ($ Millions)
Table Global Hemophilia Gene Therapy Market Size by Application (2014-2019) ($ Millions)
Table Global Hemophilia Gene Therapy Market Size Market Share by Application (2014-2019)
Figure Global Hemophilia Gene Therapy Market Size Market Share by Application (2014-2019)
Figure Global Hemophilia Gene Therapy Market Size in Hemophilia A Gene Therapy Growth Rate
Figure Global Hemophilia Gene Therapy Market Size in Hemophilia B Gene Therapy Growth Rate
Table Global Hemophilia Gene Therapy Revenue by Players (2017-2019) ($ Millions)
Table Global Hemophilia Gene Therapy Revenue Market Share by Players (2017-2019)
Figure Global Hemophilia Gene Therapy Revenue Market Share by Players in 2018
Table Global Hemophilia Gene Therapy Key Players Head office and Products Offered
Table Hemophilia Gene Therapy Concentration Ratio (CR3, CR5 and CR10) (2017-2019)
Table Global Hemophilia Gene Therapy Market Size by Regions 2014-2019 ($ Millions)
Table Global Hemophilia Gene Therapy Market Size Market Share by Regions 2014-2019
Figure Global Hemophilia Gene Therapy Market Size Market Share by Regions 2014-2019
Figure Americas Hemophilia Gene Therapy Market Size 2014-2019 ($ Millions)
Figure APAC Hemophilia Gene Therapy Market Size 2014-2019 ($ Millions)
Figure Europe Hemophilia Gene Therapy Market Size 2014-2019 ($ Millions)
Figure Middle East & Africa Hemophilia Gene Therapy Market Size 2014-2019 ($ Millions)
Table Americas Hemophilia Gene Therapy Market Size by Countries (2014-2019) ($ Millions)
Table Americas Hemophilia Gene Therapy Market Size Market Share by Countries (2014-2019)
Figure Americas Hemophilia Gene Therapy Market Size Market Share by Countries in 2018
Table Americas Hemophilia Gene Therapy Market Size by Type (2014-2019) ($ Millions)
Table Americas Hemophilia Gene Therapy Market Size Market Share by Type (2014-2019)
Figure Americas Hemophilia Gene Therapy Market Size Market Share by Type in 2018
Table Americas Hemophilia Gene Therapy Market Size by Application (2014-2019) ($ Millions)
Table Americas Hemophilia Gene Therapy Market Size Market Share by Application (2014-2019)
Figure Americas Hemophilia Gene Therapy Market Size Market Share by Application in 2018
Figure United States Hemophilia Gene Therapy Market Size Growth 2014-2019 ($ Millions)
Figure Canada Hemophilia Gene Therapy Market Size Growth 2014-2019 ($ Millions)
Figure Mexico Hemophilia Gene Therapy Market Size Growth 2014-2019 ($ Millions)
Table APAC Hemophilia Gene Therapy Market Size by Countries (2014-2019) ($ Millions)
Table APAC Hemophilia Gene Therapy Market Size Market Share by Countries (2014-2019)
Figure APAC Hemophilia Gene Therapy Market Size Market Share by Countries in 2018
Table APAC Hemophilia Gene Therapy Market Size by Type (2014-2019) ($ Millions)
Table APAC Hemophilia Gene Therapy Market Size Market Share by Type (2014-2019)
Figure APAC Hemophilia Gene Therapy Market Size Market Share by Type in 2018
Table APAC Hemophilia Gene Therapy Market Size by Application (2014-2019) ($ Millions)
Table APAC Hemophilia Gene Therapy Market Size Market Share by Application (2014-2019)
Figure APAC Hemophilia Gene Therapy Market Size Market Share by Application in 2018
Figure China Hemophilia Gene Therapy Market Size Growth 2014-2019 ($ Millions)
Figure Japan Hemophilia Gene Therapy Market Size Growth 2014-2019 ($ Millions)
Figure Korea Hemophilia Gene Therapy Market Size Growth 2014-2019 ($ Millions)
Figure Southeast Asia Hemophilia Gene Therapy Market Size Growth 2014-2019 ($ Millions)
Figure India Hemophilia Gene Therapy Market Size Growth 2014-2019 ($ Millions)
Figure Australia Hemophilia Gene Therapy Market Size Growth 2014-2019 ($ Millions)
Table Europe Hemophilia Gene Therapy Market Size by Countries (2014-2019) ($ Millions)
Table Europe Hemophilia Gene Therapy Market Size Market Share by Countries (2014-2019)
Figure Europe Hemophilia Gene Therapy Market Size Market Share by Countries in 2018
Table Europe Hemophilia Gene Therapy Market Size by Type (2014-2019) ($ Millions)
Table Europe Hemophilia Gene Therapy Market Size Market Share by Type (2014-2019)
Figure Europe Hemophilia Gene Therapy Market Size Market Share by Type in 2018
Table Europe Hemophilia Gene Therapy Market Size by Application (2014-2019) ($ Millions)
Table Europe Hemophilia Gene Therapy Market Size Market Share by Application (2014-2019)
Figure Europe Hemophilia Gene Therapy Market Size Market Share by Application in 2018
Figure Germany Hemophilia Gene Therapy Market Size Growth 2014-2019 ($ Millions)
Figure France Hemophilia Gene Therapy Market Size Growth 2014-2019 ($ Millions)
Figure UK Hemophilia Gene Therapy Market Size Growth 2014-2019 ($ Millions)
Figure Italy Hemophilia Gene Therapy Market Size Growth 2014-2019 ($ Millions)
Figure Russia Hemophilia Gene Therapy Market Size Growth 2014-2019 ($ Millions)
Figure Spain Hemophilia Gene Therapy Market Size Growth 2014-2019 ($ Millions)
Table Middle East & Africa Hemophilia Gene Therapy Market Size by Countries (2014-2019) ($ Millions)
Table Middle East & Africa Hemophilia Gene Therapy Market Size Market Share by Countries (2014-2019)
Figure Middle East & Africa Hemophilia Gene Therapy Market Size Market Share by Countries in 2018
Table Middle East & Africa Hemophilia Gene Therapy Market Size by Type (2014-2019) ($ Millions)
Table Middle East & Africa Hemophilia Gene Therapy Market Size Market Share by Type (2014-2019)
Figure Middle East & Africa Hemophilia Gene Therapy Market Size Market Share by Type in 2018
Table Middle East & Africa Hemophilia Gene Therapy Market Size by Application (2014-2019) ($ Millions)
Table Middle East & Africa Hemophilia Gene Therapy Market Size Market Share by Application (2014-2019)
Figure Middle East & Africa Hemophilia Gene Therapy Market Size Market Share by Application in 2018
Figure Egypt Hemophilia Gene Therapy Market Size Growth 2014-2019 ($ Millions)
Figure South Africa Hemophilia Gene Therapy Market Size Growth 2014-2019 ($ Millions)
Figure Israel Hemophilia Gene Therapy Market Size Growth 2014-2019 ($ Millions)
Figure Turkey Hemophilia Gene Therapy Market Size Growth 2014-2019 ($ Millions)
Figure GCC Countries Hemophilia Gene Therapy Market Size Growth 2014-2019 ($ Millions)
Figure Global Hemophilia Gene Therapy arket Size Forecast (2019-2024) ($ Millions)
Table Global Hemophilia Gene Therapy Market Size Forecast by Regions (2019-2024) ($ Millions)
Table Global Hemophilia Gene Therapy Market Size Market Share Forecast by Regions
Figure Americas Hemophilia Gene Therapy Market Size 2019-2024 ($ Millions)
Figure APAC Hemophilia Gene Therapy Market Size 2019-2024 ($ Millions)
Figure Europe Hemophilia Gene Therapy Market Size 2019-2024 ($ Millions)
Figure Middle East & Africa Hemophilia Gene Therapy Market Size 2019-2024 ($ Millions)
Figure United States Hemophilia Gene Therapy Market Size 2019-2024 ($ Millions)
Figure Canada Hemophilia Gene Therapy Market Size 2019-2024 ($ Millions)
Figure Mexico Hemophilia Gene Therapy Market Size 2019-2024 ($ Millions)
Figure Brazil Hemophilia Gene Therapy Market Size 2019-2024 ($ Millions)
Figure China Hemophilia Gene Therapy Market Size 2019-2024 ($ Millions)
Figure Japan Hemophilia Gene Therapy Market Size 2019-2024 ($ Millions)
Figure Korea Hemophilia Gene Therapy Market Size 2019-2024 ($ Millions)
Figure Southeast Asia Hemophilia Gene Therapy Market Size 2019-2024 ($ Millions)
Figure India Hemophilia Gene Therapy Market Size 2019-2024 ($ Millions)
Figure Australia Hemophilia Gene Therapy Market Size 2019-2024 ($ Millions)
Figure Germany Hemophilia Gene Therapy Market Size 2019-2024 ($ Millions)
Figure France Hemophilia Gene Therapy Market Size 2019-2024 ($ Millions)
Figure UK Hemophilia Gene Therapy Market Size 2019-2024 ($ Millions)
Figure Italy Hemophilia Gene Therapy Market Size 2019-2024 ($ Millions)
Figure Russia Hemophilia Gene Therapy Market Size 2019-2024 ($ Millions)
Figure Spain Hemophilia Gene Therapy Market Size 2019-2024 ($ Millions)
Figure Egypt Hemophilia Gene Therapy Market Size 2019-2024 ($ Millions)
Figure South Africa Hemophilia Gene Therapy Market Size 2019-2024 ($ Millions)
Figure Israel Hemophilia Gene Therapy Market Size 2019-2024 ($ Millions)
Figure Turkey Hemophilia Gene Therapy Market Size 2019-2024 ($ Millions)
Figure GCC Countries Hemophilia Gene Therapy Market Size 2019-2024 ($ Millions)
Table Global Hemophilia Gene Therapy Market Size Forecast by Type (2019-2024) ($ Millions)
Table Global Hemophilia Gene Therapy Market Size Market Share Forecast by Type (2019-2024)
Table Global Hemophilia Gene Therapy Market Size Forecast by Application (2019-2024) ($ Millions)
Table Global Hemophilia Gene Therapy Market Size Market Share Forecast by Application (2019-2024)
Table Spark Therapeutics Basic Information, Head Office, Major Market Areas and Its Competitors
Table Spark Therapeutics Hemophilia Gene Therapy Revenue and Gross Margin (2017-2019)
Figure Spark Therapeutics Hemophilia Gene Therapy Market Share (2017-2019)
Table Ultragenyx Basic Information, Head Office, Major Market Areas and Its Competitors
Table Ultragenyx Hemophilia Gene Therapy Revenue and Gross Margin (2017-2019)
Figure Ultragenyx Hemophilia Gene Therapy Market Share (2017-2019)
Table Shire PLC Basic Information, Head Office, Major Market Areas and Its Competitors
Table Shire PLC Hemophilia Gene Therapy Revenue and Gross Margin (2017-2019)
Figure Shire PLC Hemophilia Gene Therapy Market Share (2017-2019)
Table Sangamo Therapeutics Basic Information, Head Office, Major Market Areas and Its Competitors
Table Sangamo Therapeutics Hemophilia Gene Therapy Revenue and Gross Margin (2017-2019)
Figure Sangamo Therapeutics Hemophilia Gene Therapy Market Share (2017-2019)
Table Bioverativ Basic Information, Head Office, Major Market Areas and Its Competitors
Table Bioverativ Hemophilia Gene Therapy Revenue and Gross Margin (2017-2019)
Figure Bioverativ Hemophilia Gene Therapy Market Share (2017-2019)
Table BioMarin Basic Information, Head Office, Major Market Areas and Its Competitors
Table BioMarin Hemophilia Gene Therapy Revenue and Gross Margin (2017-2019)
Figure BioMarin Hemophilia Gene Therapy Market Share (2017-2019)
Table uniQure Basic Information, Head Office, Major Market Areas and Its Competitors
Table uniQure Hemophilia Gene Therapy Revenue and Gross Margin (2017-2019)
Figure uniQure Hemophilia Gene Therapy Market Share (2017-2019)
Table Freeline Therapeutics Basic Information, Head Office, Major Market Areas and Its Competitors
Table Freeline Therapeutics Hemophilia Gene Therapy Revenue and Gross Margin (2017-2019)
Figure Freeline Therapeutics Hemophilia Gene Therapy Market Share (2017-2019)

1. This report provides in depth analysis for changing competitive dynamics and keeps you ahead of competitors
2. It provides a forward looking perspective on different factors driving or restraining market growth
3. It provides a ten-year forecast assessed on the basis of how the market is expected to grow
4. It helps in making informed business decisions by having complete insights of market and by making in-depth analysis of various market segments

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